Health and Social Care Committee

Availability of Orkambi on the NHS inquiry

Inquiry status: open

The Committee has requested written submissions from NICE, NHS England and Vertex Pharmaceuticals, as can be seen in the correspondence published here.

Anyone else who would like to bring any relevant matter to the attention of the Committee should Committee staff at

Scope of the inquiry

The Committee’s inquiry into this area is currently concentrated on the provision and pricing of Orkambi, and other drugs developed by Vertex Pharmaceuticals for the treatment of cystic fibrosis. The Committee will be considering the positions taken in the ongoing negotiations between Vertex and NHS England, and NICE’s assessment of the cost-effectiveness of these drugs.


Latest evidence

  • 07 Mar 2019 - Availability of Orkambi on the NHS - oral evidence | PDF version (PDF379 KB) HC 1808 | Published 11 Mar 2019

    Evidence given by A patient representative nominated by the Cystic Fibrosis Trust, a clinician representative nominated by the Cystic Fibrosis TrustProfessor Stephen Powis, National Medical Director, John Stewart, National Director, Specialised Commissioning, NHS England, Sir Andrew Dillon, Chief Executive, Meindert Boysen, Director of the Centre for Health Technology Evaluation, NICEDr Jeff Leiden, Chairman, President and Chief Executive Officer, Stuart A. Arbuckle, Executive Vice President and Chief Commercial Officer, Vertex Pharmaceuticals

    Watch this evidence session

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